
Goals
A medical affairs team within a leading pharmaceutical company wanted to gather patient perspectives about living with a chronic, but treatable, rare disease.
The team had three primary objectives:
- Understand patient perspectives on a gene therapy clinical trial
- Obtain feedback on patient materials
- Gather input on patient education needs
Solution
11
Patients
36
Questions
10
Days
The medical affairs team decided to reach out to patient advisors via the Within3 virtual engagement platform, which would not require the patients to travel or all be available to attend a webcast at the same time. This was especially important given that patients were located in the United States, Europe, and Canada.
Patients answered multiple-choice and open-ended questions, including How willing do you think people would be to participate in the study? and How do you educate yourself and your community about your condition? Participants also used Within3’s document annotation features to provide input on patient-facing materials. During the sessions, moderators used the platform’s built-in tools to remind or encourage patients to respond to questions or contribute to the conversation.
Results
1782
Words per patient
484
Patient responses
100
Transcript pages
By using the Within3 platform, the medical affairs team achieved its objectives for the rare disease patient advisory board. With the virtual engagement approach, the medical affairs team was able to:
- Receive robust patient feedback on the observational study
- Obtain detailed responses pertaining to brochures and other patient materials
- Gather valuable insight to update patient-facing educational content